A Q&A with Cormac Maher, MD, FAANS, FAAP, FACS; Division Chief, Pediatric Neurosurgery at Stanford Medicine Children’s Health ...
Gianna Cericola from Philidelphia said the first symptoms she noticed included a burning sensation when she went to the ...
Ultragenyx Pharmaceutical RARE reported fourth-quarter 2024 loss of $1.39 per share, wider than the Zacks Consensus Estimate ...
One in 10 Americans live with a rare disease, which often lacks effective treatments. Such is the case for PIGA-CDG, an ultra ...
A four-week old baby is one of just 23 to have been diagnosed with a deadly genetic disease so rare that it has no name.