Gene therapy using modified blood stem cells helped five adults with severe hemophilia A reach therapeutic levels of clotting ...

Metagenomi says it hopes to start clinical trials next year to test MGX-001, its gene-editing therapy candidate for ...

After having a bad experience getting three vaccines at once, columnist Jennifer Lynne says that next time, she'll space them apart.

For the first time in Denmark, people with hemophilia B have been treated with the gene therapy Hemgenix (etranacogene ...

As my family started contemplating the people and routines we’ll leave behind in our upcoming job change and move, my thoughts turned to one routine in particular: For over 12 years, I’ve visited my ...

Hummingbirds offer an example to help understand people like Caeleb, who are classified as ambulatory wheelchair users. While these birds soar through the air gracefully and quickly, they must also ...

Small vesicles in the saliva of people with severe hemophilia A may explain why these patients rarely have bleeds in their mouth and throat. The vesicles contain a protein complex that’s able to ...

I hate it when the term “hero” is used to describe me and my daily life with hemophilia. Honestly, I despise it being used to describe anyone living with a rare disease or disability. I think it’s the ...